We are part of two European consortia: RiboEurope and DBAGeneCure aiming to understand the molecular basis and to develop therapeutics (gene therapy) for Diamond-Blackfan anemia (DBA).
Diamond-Blackfan anemia is a bone marrow failure syndrome manifested notably by failure to produce red blood cells.
Please watch our two educational video clips on YouTube (in Spanish and German with English subtitles) explaining in simple terms the disease and what we do.